Case Study

Innovative Technology Solution For A 15-Year Rare Disease Gene Therapy Registry

Innovative Technology Solution For A 15-Year Rare Disease Gene Therapy Registry

CASE STUDY INNOVATIVE TECHNOLOGY SOLUTION FOR A 15-YEAR RARE DISEASE GENE THERAPY REGISTRY PR A HEAL TH SCIEN CESTHE FUTURE OF CLINICAL DEVELOPMENT. PR A HEAL THSCIENCES CASE STUDY INNOVATIVE TECHNOLOGY SOLUTION FOR A 15-YEAR RARE DISEASE GENE THERAPY REGISTRY REGIONS STUDY DESCRIPTION Long-Term Prospective, Non-Interventional Follow-Up of Safety and Ecacy Registry for Pediatric Patients Treated With Gene Therapy Western Europe North Africa P

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